Summary
Alnylam Pharmaceuticals, Inc. (ALNY) has entered into a significant amendment to its Master Collaboration Agreement with Genzyme Corporation, restructuring their partnership for key RNAi therapeutic programs. This amendment grants Alnylam exclusive global rights to develop and commercialize all transthyretin (TTR) products, including the lead candidate patisiran (ALN-TTR02) and its subcutaneous counterpart ALN-TTRsc02. Conversely, Genzyme gains exclusive global rights for ALN-AT3 (fitusiran), a potential treatment for rare genetic diseases, and its backup products. This strategic realignment shifts certain financial responsibilities and potential revenue streams. Alnylam will now bear full development and commercialization costs for its TTR programs, while sharing initial costs for ALN-AT3 with Genzyme, with Genzyme taking over full financial responsibility after a specified transition period. Genzyme will provide Alnylam with a $50 million milestone payment upon the initiation of the ATLAS Phase 3 program for ALN-AT3, and Alnylam will be eligible for tiered royalties on Genzyme's sales of ALN-AT3 and its backups. Conversely, Genzyme will receive tiered royalties on Alnylam's TTR product sales outside specific territories, with varying rates depending on the product and region. This amendment aims to provide clearer development pathways and financial ownership for each company's respective key pipeline assets.
Key Highlights
- 1Alnylam secures exclusive global rights for TTR programs (patisiran, ALN-TTRsc02) from Genzyme.
- 2Genzyme receives exclusive global rights for ALN-AT3 (fitusiran) program from Alnylam.
- 3Alnylam assumes full funding responsibility for TTR product development and commercialization.
- 4Genzyme to make a $50 million milestone payment to Alnylam upon initiation of ALN-AT3 Phase 3 program (ATLAS).
- 5Alnylam eligible for tiered royalties (15-30%) on Genzyme's global net sales of ALN-AT3 and backups.
- 6Genzyme eligible for tiered royalties (up to 25%) on Alnylam's global net sales of patisiran and ALN-TTRsc02 (outside specified territories).
- 7Alnylam updates 2017 year-end cash guidance, expecting over $1.7 billion in cash, cash equivalents, marketable securities, and restricted cash.